CHOP
CHOP, Brazilian National Cancer Institute to Bring Automated Cell Therapy Manufacturing to Brazil
The institutions will use a $4 million grant to launch a Rio de Janeiro-based center equipped with an automated closed-system CAR T-cell therapy platform.
CHOP, Penn Get $14M NIH Grant to Develop Prime-Editing Treatments for Rare Metabolic Diseases
Researchers will develop therapies for urea cycle disorders and create a platform to rapidly develop treatments for other rare genetic disorders.
Gene Therapy Firm Latus Launches With $54M Series A Financing
The company will use the funds to advance gene therapies for CNS disorders such as neuronal ceroid lipofuscinosis type 2 and Huntington's disease.
After Promising Early Efficacy, Eli Lilly Eager to Study Hearing Loss Gene Therapy in More Children
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So far two patients, ages 8 and 11, have been enrolled in the Phase I/II trial of AK-OTOF, a gene therapy candidate from Lilly subsidiary Akouos.
Young Boy Can Hear After Receiving Eli Lilly's Gene Therapy, Bolstering Similar Programs
The milestone of the first deaf patient benefiting from a gene therapy is sure to spur more drug development activity in this space.
Jun 20, 2023
Jan 27, 2021