Neurological & Psychological Disorders
News on research and diagnostic developments in neuroscience.
Anew Medical Expecting to Access $54M Following SPAC Merger
The company is hoping the capital will help it advance a pipeline of gene therapies for various neurodegenerative diseases.
WashU Researchers Studying Amyloid-Lowering Insomnia Drug's Effect on Alzheimer's Development
Investigators will assess whether a drug already approved for insomnia decreases the rate of amyloid accumulation in patients at risk for developing Alzheimer's.
Bespoke Gene Therapy Consortium to 'Pressure Test' IND Roadmap with Eight Rare Disease Candidates
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The gene therapies selected by the public-private consortium will inform a playbook that walks developers through preclinical work to IND submission.
Ultragenyx to Study Angelman Syndrome Treatment in US With FDA Protocol Amendment Approval
The company can now align doses of the investigational antisense oligonucleotide therapy in pediatric patients enrolled at US and ex-US trial sites.
UniQure Selling Portion of Royalties From Hemgenix to Fund Other Gene Therapy Programs
The transaction is expected to bring in $375 million in cash that the company will use to advance gene therapies it is developing for various rare diseases.