Musculoskeletal
News on in vitro diagnostics for musculoskeletal disorders.
Belief BioMed's Duchenne Muscular Dystrophy Gene Therapy Gets FDA IND Clearance
The Shanghai-based firm will test the gene therapy candidate in patients between 4 and 9 years old with Duchenne muscular dystrophy.
Avidity Biosciences Expediting Development of AOC for Rare Muscular Dystrophy Therapy
Based on the benefits seen in facioscapulohumeral muscular dystrophy patients in a Phase I/II trial, the company said it is hoping to quickly launch registrational cohorts.
Iaso Bio Cleared to Start US Clinical Trials of CAR T-Cell Therapy in Myasthenia Gravis
The firm has already started testing equecabtagene autoleucel in China and seen promising activity in two patients.
FDA Clears Cabaletta Bio's IND to Study Cell Therapy in Myasthenia Gravis
The firm will now start a Phase I/II trial for CABA-201, which is also being explored as a potential treatment for three other autoimmune diseases.
Cartesian Therapeutics Advancing RNA-Based CAR-T in Myasthenia Gravis After Promising Early Data
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The company is betting that the novel approach will provide a better safety profile and offer more precise pharmacokinetic control than DNA-based CAR T-cell therapies.