pediatric disease
Novartis Reports Positive Data for Zolgensma in Young Adult Spinal Muscular Atrophy Population
The firm said it plans to share data with regulatory agencies from the Phase III STEER trial after it met its primary endpoint.
The Missouri hospital system designed its own 13-gene PGx panel, which it runs at its molecular genetics lab and calls the Kiddose PGx test.
Indiana University, Indiana Biosciences Research Institute Form Precision Medicine Center
The center will conduct research and advance precision medicines for diabetes, pediatric rare diseases, cancer, and Alzheimer's disease.
House E&C Committee Passes Bill on Rare Pediatric Disease Drug Development
The bill's passage through the committee improves the rare pediatric disease priority review voucher program's chances of being reauthorized before it expires Sept. 30.
D-CYPHR Launches in UK, Aiming to Improve Understanding of Childhood Health
The program will collect saliva samples for DNA analysis as well as health and lifestyle data to study how diseases develop from birth through adolescence.