alpha-1 antitrypsin deficiency

NTLA-3001 uses CRISPR to insert a healthy copy of the SERPINA1 gene, which is perturbed in alpha-1 antitrypsin deficiency.

In a bid to expand recognition and treatment of alpha-1 antitrypsin deficiency, a cause of COPD, Grifols is making its over-the-counter genetic test available for free.