Europe
Autolus Seeks FDA Approval for CAR T-Cell Therapy in B-Cell Acute Lymphoblastic Leukemia
The firm's supplemental biologics license application is based on encouraging data from a Phase II trial in more than 100 patients.
The researchers hope to reproduce in a prospective clinical trial the model's 70 percent to 80 percent accuracy for predicting immunotherapy response.
Vertex Nets European Label Expansion for Kaftrio Combo in Younger Cystic Fibrosis Patients
Vertex is also seeking to expand the Kaftrio-Kalydeco combination to cystic fibrosis patients with non-F508del Kaftrio-responsive CFTR mutations.
Germany to Test Genomics-Based Precision Medicine for Cancer, Rare Disease in National Pilot Project
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With reimbursement from public health insurance, the "model project" will run for at least five years and examine the utility of genomic sequencing for advanced cancer and rare disease patients.
Syncona Taking Freeline Therapeutics Private; Providing $15M in Financing
The additional funds will allow the company to continue to study its gene therapy in Gaucher disease and GBA1-linked Parkinson's disease.