staff reporter
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Karolinska Institutet, Cellply Partner to Improve Knowledge of NK Cell Therapies in Multiple Myeloma
Researchers will use Cellply's VivaCyte platform to conduct single-cell analyses of NK cells and evaluate their ability to treat the bone marrow cancer.
Lantern Pharma Gains FDA Clearance to Test LP-184 in Non-Small Cell Lung Cancer Subset
The firm will test the drug with immune checkpoint inhibitors in NSCLC patients with low PD-L1 expression and KEAP1 and/or STK11 mutations.
FDA Grants Regenxbio Priority Review for MPS II Gene Therapy Regulatory Application
The FDA will issue a decision on the BLA for RGX-121 by November, which if positive, could make it the first gene therapy for Hunter syndrome.
Genomate Health Raises $2M, Enters US Market With Precision Oncology Clinical Decision Support Tool
The company plans to bring its genomics-based precision oncology drug selection platform to US healthcare systems.
Hoth Therapeutics Eyeing Human Trials for HT-KIT Antisense Therapy in Early 2026
After seeing promising results in preclinical studies, the firm hopes to begin Phase I trials shortly after getting IND clearance.
Nanyang Biologics, Precisya Global Partner to Advance Personalized Medicines for Chronic Diseases
The firms will screen compounds from natural sources for activity against gene variants linked to chronic diseases.
FDA Clears Ensoma's IND to Launch Immune Disorder Gene Therapy Trial
EN-374 is a gene therapy designed to treat X-linked chronic granulomatous disease by modifying hematopoietic stem cells in vivo.
UTR Therapeutics Submits IND Application for mRNA Destabilizer
If the agency approves its application, the firm will begin a Phase I clinical trial in c-MYC-driven cancers in 2026.
Nuevocor Raises $45 Million in Series B Funding Round
The funds will support a Phase I/II trial of its gene therapy candidate in an aggressive form of dilated cardiomyopathy due to LMNA gene mutations.
In Brief This Week: MeiraGTx, IASO Biotherapeutics, Integrated DNA Technologies, Volta Labs
News items for the week of May 5, 2025.