Companies
Novartis to Seek Approval for Intrathecal SMA Gene Therapy in Children, Young Adults in Early 2025
An intravenous form of the gene therapy is already approved and sold as Zolgensma in the US for patients less than 2 years of age.
InformedDNA Acquires Coriell Life Sciences, Adds PGx Capabilities
The companies have begun integrating Coriell's PGx services into InformedDNA's DNAimpact precision health platform for payors and employers.
Patient Dies After Treatment With Sarepta's Duchenne Muscular Dystrophy Gene Therapy
The firm's stock price dropped 27 percent on Tuesday following the news that the young man died from acute liver failure after getting Elevidys.
Actinium Launches Clinical Program to Test Actimab-A With PD-1 Inhibitors in Solid Tumors
The firm will assess whether adding its CD33-targeted radiotherapy Actimab-A to PD-1 inhibitors will benefit patients more than PD-1 inhibitors alone.
A discussion at last week's Precision Medicine Tri-Con demonstrated that stakeholders are narrowing in on the challenges to realizing the promise of solid tumor MRD.