Neurological & Psychological Disorders
News on research and diagnostic developments in neuroscience.
Bluebird Bio's Skysona Continues to Benefit Patients Years Later, but Some Develop Blood Cancer
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Seven of 67 patients who received the cerebral adrenoleukodystrophy gene therapy developed blood cancer, though most cases resolved after treatment.
The field's rapid advances make securing reimbursement an important area of focus, researchers in a recent commentary argued.
MARAbio Systems Closes $19M Funding Round to Support Autism Test Commercialization
The company has developed a blood-based test to assess whether women are carriers of the antibodies that cause maternal autoantibody related-autism.
Astellas Strikes Exclusive Option Deal for AviadoBio's Frontotemporal Dementia Gene Therapy
Astellas will make a $20 million equity investment in AviadoBio for the option to exclusively develop and commercialize AVB-101.
Myrtelle to Discuss Positive Phase I/II Canavan Disease Gene Therapy Results With Regulators
The firm said it will discuss biomarker results, including a marked decrease in N-acetylaspartate levels and an increase in brain white matter.